List Of Treatable Diseases

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        DISEASE ENTITY

Viral Conditions (5)
  • HIV 1 (no AIDS diagnosis)*
  • AIDS (advanced)*
  • Hepatitis C*
  • Epstein Barr*
  • Lyme Disease*
Ocular Conditions (4)
  • Retinitis Pigmentosa*
  • Macular Degeneration*
  • Glaucoma*
  • Optic Atrophy
Endocrine diseases (4)
  • Diabetes
    • Type 2 (Adult)*
      Type 1 (Child)*
  • Adrenal Disease
  • Addison’s Disease*
  • Cushings Syndrome
Accelerated Surgery or Accident Recovery* (2)

Cardiology(4)
  • Myocardial Infarction
  • Dilated Cardiomyopathy*
  • Atherosclerosis
  • Congestive Heart Failure
Autoimmune (5)
  • Multiple sclerosis
  • Crohn’s Disease*
  • Rheumatoid Arthritis*
  • Lupus
  • Scleroderma*
Renal Disease (2)
  • Acute renal failure
  • Glomerulonephritis
Lung Disease (4)
  • Progressive Dyspnea*
  • COPD
  • Bronchial Asthma
  • Scleroderma
Neurological Disease (16)
  • Duchanne’s Muscular Dystrophy*
  • Polymyositis*
  • Multiple Sclerosis (MS)*
  • Amyotrophic Lateral Sclerosis (ALS)*
  • Parkinson’s Disease (PD)*
  • Cerebral Palsy (CP)*
  • Guilliame Barre*
  • Transverse Myelitis*
  • Basal Ganglia*
  • Supranuclear Palsy*
  • Huntington’s Disease*
  • Rhett’s Syndrome*
  • Neurological Injury
  • Acute and Chronic Stroke*
  • Spinal Cord Injury*
  • Nerve Injury*
  • Traumatic Brain Injury*
Gastroenterology (3)
  • Crohns disease
  • Liver Disease
  • Hepatitis B*
  • Hepatitis C*
Cancer (46)
  • Acute Leukemias
  • Acute Lymphoblastic Leukemia (ALL)
  • Acute Myelogenous Leukemia (AML)
  • Acute Biphenotypic Leukemia
  • Acute Undifferentiated Leukemia
  • Chronic Leukemias
  • Chronic Myelogenous Leukemia (CML)
  • Chronic Lymphocytic Leukemia (CLL)
  • Juvenile Chronic Myelogenous Leukemia (JCML)
  • Juvenile Myelomonocytic Leukemia (JMML)
  • Myelodysplastic Syndromes
  • Myelodysplastic Syndrome
  • Refractory Anemia (RA)
  • Refractory Anemia with Ringed Sideroblasts (RARS)
  • Refractory Anemia with Excess Blasts (RAEB)
  • Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
  • Chronic Myelomonocytic Leukemia (CMML)
  • Hematopoietic Cell Disorders
  • Aplastic Anemia (Severe)
  • Fanconi Anemia
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Pure Red Cell Aplasia
  • Myeloproliferative Disorders
  • Acute Myelofibrosis
  • Agnogenic Myeloid Metaplasia (myelofibrosis)
  • Polycythemia Vera
  • Essential Thrombocythemia
  • Plasma Cell Disorders
  • Multiple Myeloma
  • Plasma Cell Leukemia
  • Waldenstrom's Macroglobulinemia
  • Lymphoproliferative Disorders
  • Non-Hodgkin's Lymphoma
  • Hodgkin's Disease
  • Phagocyte Disorders
  • Acute Lympholastic Leukemia*
  • Non-Hodgkin’s Lymphoma*
  • Acute lymphocytic leukemia
  • Acute myelocytic leukemia
  • Juvenile chronic myelogenous leukemia
  • Neuroblastoma
  • Chronic myelogenous leukemia
  • Organ/Tissue Cancers (Immunotherapy)
  • Breast Cancer*
  • Prostate Cancer*
  • Colon Cancer*
  • Pancreatic Cancer*
  • Lung Cancer*
  • Malignant Melanoma*
  • Chemo Rescue*
  • Ewing Sarcoma
  • Neuroblastoma
  • Renal Cell Carcinoma
Hematology (22)
  • Chediak-Higashi Syndrome
  • Chronic Granulomatous Disease
  • Neutrophil Actin Deficiency
  • Reticular Dysgenesis
  • Anemia
  • Fanconi anemia
  • Aplastic anemia
  • Refractory anemia
  • Thalassemia
  • Sickle cell anemia
  • Amegakaryocytic thrombocytopenia
  • Kostmann syndrome
  • Blackfan-Diamond syndrome
  • Severe combined immunodeficiency
  • X-linked lymphoproliferative disorder
  • Wiskott-Aldrich syndrome
  • Hurler syndrome
  • Hunter syndrome
  • Gunther disease
  • Osteopetrosis
  • Globoid cell leukodystrophy
  • Adrenoleukodystrophy
  • Wiscott-Aldrich’s Syndrome*
Inherited Metabolic Disorders (15)
  • Mucopolysaccharidoses (MPS)
  • Hurler's Syndrome (MPS-IH)
  • Scheie Syndrome (MPS-IS)
  • Hunter's Syndrome (MPS-II)
  • Sanfilippo Syndrome (MPS-III)
  • Morquio Syndrome (MPS-IV)
  • Maroteaux-Lamy Syndrome (MPS-VI)
  • Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
  • Adrenoleukodystrophy
  • Mucolipidosis II (I-cell Disease)
  • Krabbe Disease
  • Gaucher's Disease
  • Niemann-Pick Disease
  • Wolman Disease
  • Metachromatic Leukodystrophy
Histiocytic Disorders (4)
  • Familial Erythrophagocytic Lymphohistiocytosis
  • Histiocytosis-X
  • Hemophagocytosis
Inherited Immune System Disorders (13)
  • Ataxia-Telangiectasia
  • Kostmann Syndrome
  • Leukocyte Adhesion Deficiency
  • DiGeorge Syndrome
  • Bare Lymphocyte Syndrome
  • Omenn's Syndrome
  • Severe Combined Immunodeficiency (SCID)
  • SCID with Adenosine Deaminase Deficiency
  • Absence of T & B Cells SCID
  • Absence of T Cells, Normal B Cell SCID
  • Common Variable Immunodeficiency
  • Wiskott-Aldrich Syndrome
  • X-Linked Lymphoproliferative Disorder
Other Inherited Disorders (4)
  • Lesch-Nyhan Syndrome
  • Cartilage-Hair Hypoplasia
  • Glanzmann Thrombasthenia
  • Inherited Platelet Abnormalities

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